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2024 Annual Meeting | SS10 - Â鶹´«Ã½Ó³»­ Section Spotlight: Gene Therapies in Human Clinical Trials for CNS Diseases

Tuesday 04/16/24
03:00 PM - 04:00 PM MDT Add To Calendar
This program will be presented in-person only
This program is not expected to be available in the meeting's On Demand product.
Other
Sonika Agarwal, MD, FÂ鶹´«Ã½Ó³»­, Samuel A. Frank, MD, FÂ鶹´«Ã½Ó³»­, Donald Gilbert, MD, FÂ鶹´«Ã½Ó³»­, Deepa S. Rajan, MD, FÂ鶹´«Ã½Ó³»­, Lauren Reoma, MD, FÂ鶹´«Ã½Ó³»­
Child Neurology and Developmental Neurology, General Neurology
Sponsored by the Child Neurology Section in collaboration with the Neurogenetics and Experimental Neurotherapeutics Sections. Participants should be able to describe basic mechanisms of gene therapies such as lentiviral vectors, adeno-associated viral vectors, and antisense oligonucleotides recently/currently in human clinical trials for application in central nervous system diseases; and discuss successes, failures, and treatments on the horizon for severe neurogenetic diseases in children and adults.
0.00 CME credit
Patient Care & Procedural Skills, Practice-based Learning and Improvement, Systems-based Practice, Quality Improvement
Advanced
Fellow, Resident, General Neurologist, Specialist Neurologist, Non-neurologist, Advanced Practice Provider, Neurohospitalist, Medical Student
Case-based, Didactic, Audience Participation
Event Timeline
03:00 PM - 04:00 PM MDT Discussion Â鶹´«Ã½Ó³»­ Section Spotlight: Gene Therapies in Human Clinical Trials for CNS Diseases
Samuel A. Frank, MD, FÂ鶹´«Ã½Ó³»­, Donald Gilbert, MD, FÂ鶹´«Ã½Ó³»­, Deepa S. Rajan, MD, FÂ鶹´«Ã½Ó³»­
Faculty Disclosures
Sonika Agarwal, MD, FÂ鶹´«Ã½Ó³»­ Dr. Agarwal has nothing to disclose.
Samuel A. Frank, MD, FÂ鶹´«Ã½Ó³»­ Dr. Frank has received personal compensation in the range of $500-$4,999 for serving as a Consultant for uniQure. Dr. Frank has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Teva. Dr. Frank has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Roche. The institution of Dr. Frank has received research support from Huntington's Disease Society of America. The institution of Dr. Frank has received research support from Roche/Genentech. The institution of Dr. Frank has received research support from CHDI Foundation. The institution of Dr. Frank has received research support from Huntington Study Group. The institution of Dr. Frank has received research support from Cerevel.
Donald Gilbert, MD, FÂ鶹´«Ã½Ó³»­ Dr. Gilbert has received personal compensation in the range of $500-$4,999 for serving as a Consultant for PTC Therapeutics. Dr. Gilbert has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Illumina. Dr. Gilbert has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Emalex Biosciences. The institution of Dr. Gilbert has received research support from NIMH. The institution of Dr. Gilbert has received research support from Emalex Biosciences. The institution of Dr. Gilbert has received research support from PTC Therapeutics. The institution of Dr. Gilbert has received research support from Department of Defense. The institution of Dr. Gilbert has received research support from Quince Therapeutics. Dr. Gilbert has received publishing royalties from a publication relating to health care. Dr. Gilbert has received publishing royalties from a publication relating to health care. Dr. Gilbert has received personal compensation in the range of $500-$4,999 for serving as a Medical Second Opinion Expert with Teldoc/Advanced Medical. Dr. Gilbert has received personal compensation in the range of $10,000-$49,999 for serving as a Medical Expert with Department of Health and Human Services/Vaccine Injury Compensation Program.
Deepa S. Rajan, MD, FÂ鶹´«Ã½Ó³»­ Dr. Rajan has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Takeda. Dr. Rajan has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Sanofi. Dr. Rajan has received personal compensation in the range of $0-$499 for serving as an Editor, Associate Editor, or Editorial Advisory Board Member for Medlink Neurology. The institution of Dr. Rajan has received research support from National Scleroderma Foundation. The institution of Dr. Rajan has received research support from Denali Therapeutics. The institution of Dr. Rajan has received research support from Ultragenyx . The institution of Dr. Rajan has received research support from Regenxbio. The institution of Dr. Rajan has received research support from Takeda. The institution of Dr. Rajan has received research support from Prevail Therapeutics. The institution of Dr. Rajan has received research support from Children's Neuroscience Institute. Dr. Rajan has received intellectual property interests from a discovery or technology relating to health care.
Lauren Reoma, MD, FÂ鶹´«Ã½Ó³»­ Dr. Reoma has received research support from NIH. Dr. Reoma has a non-compensated relationship as a Vice Chair with Â鶹´«Ã½Ó³»­ Experimental Neurotherapeutics Section that is relevant to Â鶹´«Ã½Ó³»­ interests or activities. Dr. Reoma has a non-compensated relationship as a Federal Employee with NINDS/NIH that is relevant to Â鶹´«Ã½Ó³»­ interests or activities. Dr. Reoma has a non-compensated relationship as a Member with ASENT Program Committee that is relevant to Â鶹´«Ã½Ó³»­ interests or activities.